E-Poster Presentation 34th Lorne Cancer Conference 2022

Pdcsm-cancer: using graph-based signatures to identify small molecules with anticancer properties (#308)

Raghad Al Jarf 1 2 3 4 , Alex G. C. de Sá 1 2 3 4 5 , Douglas E. V. Pires 1 2 3 4 6 , David B. Ascher 1 2 3 4 5 7
  1. University of Melbourne, Parkville, VIC, Australia
  2. Structural Biology and Bioinformatics, Department of Biochemistry, The Bio21 Molecular Science and Biotechnology Institute University of Melbourne, Melbourne, Victoria, Australia
  3. Computational Biology and Clinical Informatics, Baker Heart and Diabetes Institute, Melbourne, Victoria, Australia
  4. Systems and Computational Biology, Bio21 Institute, University of Melbourne, 30 Flemington Rd, Parkville VIC 3052
  5. Baker Department of Cardiometabolic Health, Melbourne Medical School, University of Melbourne, Parkville 3010, VIC, Australia
  6. School of Computing and Information Systems, University of Melbourne, Parkville 3010, VIC, Australia
  7. Department of Biochemistry, University of Cambridge, 80 Tennis Ct Rd, Cambridge CB2 1GA

The development of new, effective, and safe drugs to treat cancer remains a challenging and time-consuming task due to limited hit rates, restraining subsequent development efforts. Despite the impressive progress of quantitative structure-activity relationship and machine learning-based models that have been developed to predict molecule pharmacodynamics and bioactivity, they have had mixed success at identifying compounds with anticancer properties against multiple cell lines. Here, we have developed a novel predictive tool, pdCSM-cancer, which uses a graph-based signature representation of the chemical structure of a small molecule in order to accurately predict molecules likely to be active against one or multiple cancer cell lines. pdCSM-cancer represents the most comprehensive anticancer bioactivity prediction platform developed till date, comprising trained and validated models on experimental data of the growth inhibition concentration (GI50%) effects, including over 18,000 compounds, on 9 tumor types and 74 distinct cancer cell lines. Across 10-fold cross-validation, it achieved Pearson’s correlation coefficients of up to 0.74 and comparable performance of up to 0.67 across independent, non-redundant blind tests. Leveraging the insights from these cell line-specific models, we developed a generic predictive model to identify molecules active in at least 60 cell lines. Our final model achieved an area under the receiver operating characteristic curve (AUC) of up to 0.94 on 10-fold cross-validation and up to 0.94 on independent non-redundant blind tests, outperforming alternative approaches. We believe that our predictive tool will provide a valuable resource to optimizing and enriching screening libraries for the identification of effective and safe anticancer molecules. To provide a simple and integrated platform to rapidly screen for potential biologically active molecules with favorable anticancer properties, we made pdCSM-cancer freely available online at http://biosig.unimelb.edu.au/pdcsm_cancer.